The challenge of treating patients with genetic disorders in which a single mutated gene is simply too large to be replaced using traditional gene therapy techniques may soon be a thing of the past. A Nationwide Children’s Hospital study describes a new gene therapy approach capable of delivering full-length versions of large genes and improving skeletal muscle function Continue reading
Tag Archives: dystrophy-type
New gene transfer strategy shows promise for limb girdle and other muscular dystrophies
Public release date: 9-Jul-2012 [ | E-mail | Share ] Contact: Erin Pope Erin.Pope@NationwideChildrens.org 614-355-0495 Nationwide Children’s Hospital The challenge of treating patients with genetic disorders in which a single mutated gene is simply too large to be replaced using traditional gene therapy techniques may soon be a thing of the past. A Nationwide Children’s Hospital study describes a new gene therapy approach capable of delivering full-length versions of large genes and improving skeletal muscle function. Continue reading